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gene therapy

A strategic agreement has been signed by GlaxoSmithKline (GSK) and Orchard Therapeutics, involving the transfer of GSK’s portfolio of approved and investigational rare disease gene therapies to Orchard. more

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TrakCel, software developer for gene therapy supply chain tracking and orchestration, has announced it will be organisation that is responsible for tracking and documentation of cell and gene therapy products for the Northern Alliance more

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Healthcare solutions provider, Novartis, is set to gain further ground in the area of gene therapy through its agreement to acquire AveXis — US-based clinical stage gene therapy company — for $8.7 billion. more

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Cell & Gene Therapies: A guide to single-use fluid connections more

Biochromatography development and manufacturing company, BIA Separations, and biotech, RBPS Technology, have signed a partnership agreement to support the clinical-stage production of high purity Minicircle DNA for viral and non-viral gene transfer more

Technology

A partnership agreement has been signed by BIA Separations, a biochromatography development and manufacturing company, and Nuvonis Technologies, a biotech company, to support the production of vaccine and gene therapy. more

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Gene control company, Synpromics, has announced it will collaborate with the University College London (UCL) Great Ormond Street Institute of Child Health for the development of novel gene therapies for pathologies affecting the haematopoietic system more

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German-based company, SIRION Biotech has signed a two-year development agreement with a clinical-stage ophthalmology company, Acucela, to establish optimised adeno associated virus (AAV) vectors for clinical applications in ocular gene therapy. more

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US-based company, Spark Therapeutics, has announced a programme of improved access to its one-time gene therapy treatment, LUXTURNA, indicated for the treatment of patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy more

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Lonza and Massachusetts Eye and Ear (MEE) have granted Akouos (a new biotechnology company) licences for exclusive rights to the ancestral adeno-associated viral vectors (Anc-AAV) gene therapy platform for all hearing and balance disorders. more

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Gene control company, Synpromics, has revealed its collaboration with University College London (UCL) for the generation of a range of synthetic gene promotors for the central nervous system (CNS) to develop a therapy for Parkinson’s disease. more

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CEVEC Pharmaceuticals has been granted a patent for its expression technology CAP-Go, strengthening the company’s position in producing recombinant proteins with tailor-made glycosylation. more

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A clinical-stage biopharmaceutical company, Abeona Therapeutics, has announced a collaborative agreement between nine Sanfilippo foundations to provide grants for the advancement of its gene therapy programme. more

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Frost & Sullivan is to host a webinar on stem cell therapy pipeline and treatments innovating regenerative medicine more

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Yet another doping story to hit the mainstream media headlines; this time concerning a data leak that, according to the Sunday Times paper, reveals the "extraordinary extent of cheating" at the world's most prestigious sporting events. more

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A major GMP inspection has successfully concluded for apceth's production facilities. The GMP inspection was conducted by the Bavarian state authorities and the Germany regulatory agency Paul-Ehrlich-Institute more

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Fibrocell Science and Intrexon have announced positive in vitro pre-clinical data for Fibrocell's lead orphan gene-therapy drug candidate for the treatment of recessive dystrophic epidermolysis bullosa. more

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Sigma-Aldrich Corporation’s custom manufacturing business unit, SAFC Commercial, has announced the strategic expansion of its existing facility in Carlsbad, California. more

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