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sickle cell disease

A study, recently published in Nature Medicine, has demonstrated that a novel mutant enzyme may offer potential for medical use in the treatment of sickle cell disease (SCD). more

News

HealthCap, a European venture capital firm, has invested SEK 60 million into the portfolio company of Karolinska Development — Modus Therapeutics. more

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The US Food and Drug Administration (FDA) has approved Addmedica’s drug Siklos (hydroxyurea tablets) for the treatment of paediatric patients, two years of age and older, suffering from sickle cell anaemia. more

Technology

The US Food and Drug Administration (FDA) has approved Endari (L-glutamine oral powder), a treatment for patients aged five years and older with sickle cell disease, which reduces severe complications associated with the blood disorder. more

News

A new Managed Access Program (MAP) for the treatment of sickle cell disease has been announced for Emmaus Life Sciences’ pharmaceutical grade L-glutamine treatment (PGLG). more

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